Clinical Trial NCT06449001

Trial

Alexion – ALXN2040-PNH-302 (NCT06449001)

Clinical trial ID

NCT06449001

Drug name

ALXN2040

Company:

Alexion Pharmaceuticals, Inc.

Drug trade name

Danicopan

Clinicaltrials.gov

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Phase of study

3

Current status

Recruiting

Start

30/09/2025

Substance

Danicopan (oral add‑on to ravulizumab or eculizumab)

Research question

Evaluate efficacy of danicopan as add‑on to ravulizumab or eculizumab in pediatric participants with PNH and clinically significant extravascular hemolysis

Delivery method of drug

Frequency

Clinical trial locations

France, UK